2025 Speakers Alice Stanton Assistant Professor at Harvard Medical School and MGH Harvard Medical School Aron Kos Principal Scientist ProQR Avery Yan CEO Riboway Therapeutics Bruce Morimoto Principal Consultant Principal Consultant Damon Wang CEO Nucyrna Therapeutics Dan Tardiff Senior Vice President & Head of Discovery CAMP4 Therapeutics Deepak Sampath Senior Vice President Head of Research Ultragenyx Pharmaceuticals Hagen Cramer Chief Technology Officer QurAlis Corp. Hideaki Tomita Group Leader Luxna Biotech Ioana Panait Senior Researcher Beacon Research Operations, Hanson Wade Jan Grunewald Associate Director AstraZeneca Jimmy Weterings Vice President & Head of Oligonucleotide Therapeutics Bonito Biosciences Jurek Kozyra Founder Chief Executive Officer Nanovery Ltd. Kathrin Meyer Chief Scientific Officer Alcyone Therapeutics Leo Qian Co-Founder & Vice President - Discovery Research Entrada Therapeutics Marjie Hard Senior VP, Development Sciences Trace Neuroscience Meena . SVP Stoke Therapeutics Mohammad Shadid, PhD, MBA Vice President - Preclinical & Translational Sciences Korro Bio Muthiah Manoharan SVP Alnylam Pharmaceuticals Naim Nazef Vice President, Oligonucleotide Chemistry Denali Therapeutics Neelroop Parikshak Director, Next Wave Research Alnylam Pharmaceutical Nicole Lykens Director - Neurobiology Novo Nordisk Padma Akkapeddi Senior Scientist Denali Therapeutics Puneet Anand Senior Principal Scientist - Genetic Medicines Regeneron Pharmaceuticals Ron Wange Principal Consultant USA FDA (formerly) Scott V. Dindot Executive Director of Molecular Genetics Ultragenyx Pharmaceuticals Setsu Endoh-Yamagami Senior scientist / Manager FUJIFILM Healthcare Americas Corporation Stefano Zanotti Senior Vice President, Head of Neuromuscular Research Dyne Therapeutics Sudhir Agrawal Founder & President University of Massachusetts Medical School Tracy Stone Principal Scientist ProteinQure 2025 PROGRAM REGISTER INTEREST PARTNER