Speakers Alice Stanton Assistant Professor Massachusetts Institute of Technology Bruce Morimoto Principal Consultant Principal Consultant Deepak Sampath Senior Vice President, Head of Research Ultragenyx Pharmaceuticals Fay Touti Director - Oligonucleotide & Conjugation Chemistry Apellis Pharmaceuticals Gerard Platenburg Chief Scientific Officer ProQR Helene Tran Director Servier Hideaki Tomita Group Leader (Biology) Luxna Biotech Ioana Panait Senior Researcher Beacon Research Operations, Hanson Wade Irina Antonijevic Chief Medical Officer Trace Neuroscience Jan Grunewald Associate Director AstraZeneca Jim Weterings Vice President, Head of Oligonucleotide Therapeutics Bonito Biosciences Julie Garlick Scientist 3 Genentech Kathrin Meyer Chief Scientific Officer & Head of R&D Alcyone Therapeutics Meena – Senior Vice President, Translational DMPK & Clinical Pharmacology Stoke Therapeutics MUTHIAH (Mano) MANOHARAN SVP Alnylam Pharmaceuticals Naim Nazef Vice President, Oligonucleotide Chemistry Denali Therapeutics Nicole Lykens Director - Neurobiology Novo Nordisk Paul Nioi Senior Vice President, Research Alnylam Pharmaceuticals Puneet Anand Senior Principal Scientist - Genetic Medicines Regeneron Ron Wange Associate Director of Pharmacology & Toxicology USA FDA (formerly) Scott Dindot Professor Ultragenyx Pharmaceuticals Stefano Zanotti Vice President of Neuromuscular Research Dyne Therapeutics VIEW PROGRAM REGISTER PARTNER