Stefano Zanotti

Company: Dyne Therapeutics

Job title: Senior Vice President, Head of Neuromuscular Research

Seminars:

TfR1-Mediated Delivery of Oligonucleotides to Address Neuromuscular Diseases: Translating Research into Clinical Functional Improvement 10:50 am

The FORCE™ platform leverages Transferrin Receptor 1 (TfR1) to enable delivery of therapeutic oligonucleotides to muscle and the CNS Discuss preclinical data in models of DM1 and DMD to demonstrate that FORCE™ delivers broad functional improvement in muscle and CNS phenotypes The FORCE™ platform achieved POC in the ACHIEVE and DELIVER trials in DM1 and…Read more

day: Day 1