Dan Tardiff

Company: CAMP4 Therapeutics

Job title: Senior Vice President & Head of Discovery

Seminars:

Targeting Regulatory RNAs with Antisense Oligonucleotides for the Potential Treatment of SYNGAP1-Related Disorders 10:30 am

Antisense oligonucleotides target non-coding regulatory RNAs to boost gene expression in haploinsufficient CNS diseases Unique modality enabling functional protein restoration without gene editing or replacement Lead program in SYNGAP1-related disorders has disease-modifying potential to broadly address disease symptoms Preclinical data show efficacy in a humanized mouse model and increased SynGAP protein in non-human primates with…Read more

day: Day 2