SCAD Platform for the Delivery of Duplex RNA to the CNS
Time: 11:00 am
day: Conference Day One
Details:
- SCAD (smart chemistry-aided delivery) is a simple yet effective platform for delivering duplex RNA including siRNA and saRNA to the CNS via intrathecal administration
- SCAD delivered siRNA can achieve profound and durable target gene knockdown in rodents, nonhuman primates and human
- SCAD platform has demonstrated a very favorable safety profile
