Leveraging Humanized Preclinical Models for the Rapid Optimization of UNC13A ASOs on AcuraStem’s iNeuroRx® Technology Platform
Time: 4:00 pm
day: Conference Day One
Details:
- Exploring UNC13A biology in treating ALS & FTD
- Utilizing accurate patient-derived hIPSC models of UNC13A pathology to optimize UNC13A ASOs
- Utilizing humanized UNC13A mice to understand exposure and target engagement of UNC13A ASOs
